Conference Program
08:00
Registration
09:00
Conference Opening & Welcome
Philippe Carteron de Balmont - Conference Chair
09:30-10:30
Session 1: WHERE ARE WE
Led by Eurordis
09:30-10:30
Rare Disease Expertise and Orphan Drug Experience in Europe since 1999
10:30-11:00
Coffee Break, Networking & Visit the Exhibition
11:00-12:30
Session 2: SUCCESS FACTORS (1)
Led by Philippe Carteron
Identifying all stakeholders
Patients identification
Building relationships with patient group
Expert groups
Developing disease awareness
12:30-13:30
Lunch Break, Poster Viewing & Visit the Exhibition
13:30-15:00
Session 3: DO NOT REINVENT THE WHEEL
Orphanet Session
14:00-15:00
Session 4: SUCCESS FACTORS (2)
Led by Philippe Carteron
Creating European registries
Strategically selecting trial sites
Shall companies multiply sites all over Europe?
15:00-15:30
Coffee Break, Networking & Visit the Exhibition
15:30-16:30
Session 5: RARE DISEASES PATIENTS ELIGIBLE ARE EVEN RARER
Led by Philippe Carteron
Conducting trans-border clinical trials across Europe
Understanding clinical trial landscape beyond “big 5 countries”
Avoiding pitfalls and optimizing orphan drug development
16:30-17:00
Panel Discussion and Q&A
17:00
End of Day One
08:30
Registration
09:00-10:30
Session 6: EARLY ACCESS at WHICH POINT AND WHERE
Led by Philippe Carteron
Preparing for pre-launch activities including early access programs in Europe (Compassionate use and named patient programs).
10:00-10:30
Session 7: LOGISTIC
Orphan Drug CT and pre-launch Logistics
10:30-11:00
Coffee Break, Networking & Visit the Exhibition
11:00-12:30
Session 8: EARLY ACCESS IN PRACTICE
Led by Philippe Carteron
12:30-13:30
Lunch Break, Networking & Visit the Exhibition
13:30-14:30
Session 9: THE FUTURE OF ORPHAN DRUGS
Panel Discussion
14:30-15:00
CLOSING REMARKS AND TAKEAWAYS
Philippe Carteron de Balmont - Conference Chair
15:00-15:30
Coffee Break, Networking & Exhibition
15:30
End of Conference
